Learn about the global clinical trial for sickle cell disease aimed at improving quality of life and addressing anemia.

Serenity Cole enjoyed Christmas last month relaxing with her family near her St. Louis home, making crafts and visiting ...

Columnist Michelle Harlan, who's currently taking hydroxyurea to treat her sickle beta-zero thalassemia, considers some other ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

A year ago, NBC News joined Wedam Minyila as he began undergoing a groundbreaking treatment for sickle cell disease. The process has included having his stem cells removed for a revolutionary gene ...

Motixafortide alone and in combination with natalizumab can support the collection of the large number of stem cells required by gene therapies for sickle cell disease within a single apheresis cycle ...

Motixafortide effectively mobilized sufficient hematopoietic stem cells (HSCs) in patients with sickle cell disease enabling accelerated access to gene therapies 90% (9 of 10) of patients were able to ...