Under the agreement, participating states will receive “discounts and rebates” from the drugmakers if the treatments don’t ...

After 35 years of consistent pain, Allan Byamukama became one of the few individuals in the world cured of sickle cell disease through gene therapy. Born in Uganda and diagnosed with sickle cell ...

A new CRISPR-based one-off procedure that lowers "bad" cholesterol has been approved to enter Phase I human trial. If ...

For the first time, the tools to rewrite human biology are moving from speculative fiction into regulated clinics and ...

Columnist Michelle Harlan, who's currently taking hydroxyurea to treat her sickle beta-zero thalassemia, considers some other ...

Join the ELRIG conference to hear from experts on cell and gene therapy. Discover advancements shaping the future of medicine.

The market size of CGT products is expected to continue to rise by 2031 and reach $63 billion. CGTs have yielded commercial gains for several pharma companies. For example, some of the top-selling CGT ...

Caring Cross, a 501(c)(3) non-profit dedicated to improving access to advanced therapies, and Boston Children's Hospital today announced a collaboration to provide a sustainable, affordable pathway ...

The government is using sickle cell treatments to test a new strategy: paying only if the therapies benefit patients.

NEW YORK – Boston Children's Hospital has granted a worldwide license for an investigational gene therapy for sickle cell disease and beta thalassemia to Caring Cross, the nonprofit announced this ...

Caring Cross, a 501(c)(3) non-profit dedicated to improving access to advanced therapies, and Boston Children’s Hospital have announced a collaboration to provide a sustainable, affordable pathway for ...