Picture CRISPR-Cas9, a gene editing technology, as a GPS-guided scalpel: gRNA directs the Cas9 enzyme, a protein that cuts ...

Organ transplants are a "never-ending tragedy," with referrals steadily going up while the number of organs available remains ...

Most days, our bodies are just there—mundane vessels we inhabit on autopilot. We wake up, get on with our routines, eat, sleep, repeat. But the moment you actually stop and think about what’s ...

Day to day, we exist in our bodies without thinking much about them. We wake up, eat, move around, and fall asleep again, all ...

A Black female doctor when that was rare, she developed a diagnostic test for the disease that is still a standard tool, as ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

Memantine, a long-approved and cost-effective drug used to treat Alzheimer’s disease, could also benefit patients with sickle cell anemia in the future. Initial clinical data from an international ...

Why Elon Musk says saving for retirement will be 'irrelevant' in the next 20 years Welcome to Greenland, an economy reliant on subsidies and shrimp 17 college basketball players charged in ...

The year ahead feels like a long stretch of unwrapped gifts. Some days are bright boxes with bows; others are wrinkled wrapping paper hiding something unexpected. For me, living with sickle cell ...

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

When asked to picture the ideal cure for sickle-cell disease, molecular biologist Stefano Rivella, a researcher at Children’s Hospital of Philadelphia (CHOP), Pennsylvania, didn’t gaze into the ...

Caring Cross, a 501(c)(3) non-profit dedicated to improving access to advanced therapies, and Boston Children's Hospital today announced a collaboration to provide a sustainable, affordable pathway ...