Sebastien Beauzile, 21, has been cured of sickle cell anemia, according to his doctors at Cohen’s Children’s Medical Center. Beauzile received a new gene therapy called Lyfgeni, created by the biotech ...

Two FDA-approved gene therapies, Lyfgenia and Casgevy, will be offered through an outcomes-based Medicaid model launching in January 2025. The initiative ties payments to treatment effectiveness, ...

SOMERVILLE, Mass.--(BUSINESS WIRE)--bluebird bio, Inc. (Nasdaq: BLUE) today announced that new and updated data from its lentiviral vector (LVV) gene addition programs in patients with sickle cell ...

Stable production of anti-sickling adult hemoglobin (HBA T87Q) and elimination or significant reduction of vaso-occlusive events sustained through last follow-up for all evaluable patients (n=38), ...

A 21-year-old man has become the first person in New York—and one of the first in the world—to be cured of sickle cell anemia. A novel form of gene therapy enabled the man to receive a life-changing ...

A Black female doctor when that was rare, she developed a diagnostic test for the disease that is still a standard tool, as well as treatment guidelines.

Sickle cell anemia causes sickle-shaped cells to block blood flow to the lungs, leading to acute chest syndrome. Common treatment methods involve oxygen supplementation and pain management. Sickle ...

Sickle cell anemia refers to a group of genetic blood disorders that affect a person’s levels of hemoglobin, the protein in ...

Sickle cell anemia may qualify as a disability for people experiencing severe symptoms, allowing access to benefits. However, eligibility depends on how the condition affects daily life. Sickle cell ...

Sickle cell disease (SCD) is a group of genetic blood disorders. A person inherits SCD from their parents when they inherit two copies of the sickle cell gene, one from each parent. This hereditary ...

When Amy Cohen, 29, finished the New York City Marathon, she broke ground as the first person with the illness to run the 26.2 mile race Mass General Brigham Amy Cohen became the first-ever person ...