Sickle cell patients and their families are speaking out, saying their pain is being treated with a one-size-fits-all ...

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

Under the agreement, participating states will receive “discounts and rebates” from the drugmakers if the treatments don’t ...

A Black female doctor when that was rare, she developed a diagnostic test for the disease that is still a standard tool, as ...

If you or someone you know has sickle cell disease (SCD), you may have heard of Lyfgenia, one of two gene therapies approved for this condition. Gene therapies are the only treatments for SCD that can ...

A year ago, NBC News joined Wedam Minyila as he began undergoing a groundbreaking treatment for sickle cell disease. The process has included having his stem cells removed for a revolutionary gene ...

After spending a year living within the walls of Boston Children's Hospital fighting sickle cell disease, Jayden Wilsey, 15, finally emerged on Sept. 15 — free from the pain associated with the ...

In November 2023, the UK became the first country in the world to authorise a Crispr gene-editing therapy.

A new gene therapy for people who can have a stem cell transplant but do not have a suitable donor has been approved.

This video is no longer available. It is described as intense pain shooting throughout your body and has had a history of misdiagnosis and complications as patients are constantly traveling to ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

After 35 years of consistent pain, Allan Byamukama became one of the few individuals in the world cured of sickle cell ...