Farrell High School students are raising awareness for an important cause--donating blood for sickle cell anemia.

Sickle cell disease is caused by a single genetic mutation that alters the shape of red blood cells. While the condition causes severe pain and health complications, carriers gain resistance to ...

In November 2023, the UK became the first country in the world to authorise a Crispr gene-editing therapy.

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

The lifelong effects of rare blood disorder diagnoses in childhood are being analysed in a first-of-its-kind study led by the ...

A new gene therapy for people who can have a stem cell transplant but do not have a suitable donor has been approved.

At 3 months old, Victoria Gray wouldn’t stop crying. Blood tests brought devastating news: she had sickle cell disease, a genetic blood disorder that blocks blood flow and oxygen delivery to the body.

Few companies stand better poised than Beam Therapeutics to reap the first fruits of the FDA’s promised flexibility toward cell and gene therapies. | Riding a regulatory win for its base editing ...

Biomarker testing is crucial for personalized oncology care, aiding in risk stratification and treatment decisions, but faces ...

Campaigners welcomed a decision to approve a new weekly injection to treat those with severe haemophilia B for use by the NHS ...

IVF allows parents to choose embryos with the least harmful genetic makeup, helping prevent rare or debilitating genetic ...

Arguably, the most important thing you can have in this life is your health. No matter how much money you have or resources ...