Sickle cell disease is caused by a single genetic mutation that alters the shape of red blood cells. While the condition ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

Memantine, a long-approved and cost-effective drug used to treat Alzheimer’s disease, could also benefit patients with sickle cell anemia in the future. Initial clinical data from an international ...

Every day, human bone marrow produces around 200 billion new red blood cells. 1 But in five to seven out of every million people, that system is severely disrupted. 2 The result is Diamond-Blackfan ...