Rare diseases often require urgent access to life-saving therapies for affected children. Families face regulatory delays for treatment, while children lose ground in irreversible ways. Proposed ...

A handful of small, early-stage clinical trials are investigating whether CAR-T therapy can improve symptoms in multiple ...

Can the right diet "cure" schizophrenia? Despite provocative case studies, research to date indicates we do not know.

A young YouTuber and royal reporter has opened up about living with an autoimmune condition she says “broke” her during her school years.

India: A review published in the European Journal of Medical Research highlights that Coeliac Disease can significantly affect the musculoskeletal system, leading to bone, muscle, and ...

Coeliac disease affects approximately 1·4% of the global population.1 It is the only autoimmune gastrointestinal disorder for which the environmental trigger (gluten) is known. Treatment relies ...

How, 16, from Liverpool, was diagnosed with Friedreich's Ataxia in 2025 - a life-limiting disorder that progressively damages ...

WOODBRIDGE, Conn.--(BUSINESS WIRE)--Cure Rare Disease (CRD), a non-profit biotechnology organization, today announced a landmark partnership with the LGMD2L Foundation. This collaboration is backed by ...

Cure Rare Disease (CRD), a non-profit biotechnology organization, today announced a landmark partnership with the LGMD2L Foundation. This collaboration is backed by a generous commitment of $7.65 ...

LONG ISLAND (PIX11) – A Long Island single mother is sharing her 2-year-old daughter’s medical story in hopes of finding a cure for a disease that has caused multiple aneurysms to grow. With the ...

ROCK HILL, S.C. — Just days after her son was born, Julia Friar learned he had galactosemia, a rare genetic disorder that can be life-threatening. Three years later, the Rock Hill mother is channeling ...

Every Cure, a biotech nonprofit started by a University of Pennsylvania researcher, has landed $76 million in federal funding to advance its artificial intelligence match-making tool that identifies ...