The evidence for Elevidys is growing, and Sarepta is working to make the DMD treatment widely available, the company's ...

Columnist Shalom Lim is using his lived experience with Duchenne muscular dystrophy to consult with organizations about ...

Dyne Therapeutics' Z-basivarsen led to gains in motor function and cognition for myotonic dystrophy type 1, and is entering a ...

Columnist Robin Stemple knows that his physical challenges aren't his fault, but that doesn't make it any easier to avoid ...

New presentations at MDA 2026 expand the understanding of how Duvyzat may help people with Duchenne muscular dystrophy.

PGN-EDODM1, an experimental DM1 therapy from Pepgen, showed biomarker activity and splicing correction in an early clinical ...

MDA 2026 keynote speaker John Crowley discussed with MD News Today the progress made in neuromuscular disease and the future ...

Columnist Betty Vertin says her three sons with DMD may not have a big social life, but they have a big family that makes up for it.

Capricor has reapplied for FDA approval of deramiocel, its therapy for DMD-related heart disease, and expects a decision by August 22.