Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell disease (SCD) patients to access the CRISPR/Cas9 gene-edited therapy, CASGEVY® ...
The bottom line is few companies can match its combination of established leadership in rare diseases and realistic pathways ...
People in England with sickle cell will be able to get the world’s first CRISPR-based medicine under an agreement between the ...